CRISPR Gene Editing In Treating Leber Congenital Amaurosis and Antibody Developed To Prevent Ceramide Buildup In Treating Diabetic Retinopathy

Dr. Mark Pennesi (Oregon Health and Science University - Portland, OR)

Dr. Julia Busik (University of Oklahoma College of Medicine - Oklahoma City, OK)

Dr. Mark Pennesi, Director of Ophthalmic Genetics at the Retina Foundation of the Southwest, in Dallas, Professor of Ophthalmology at Oregon Health and Science University, Casey Eye Institute, in Portland, explains how CRISPR gene editing helped some Leber Congenital Amaurosis patients in a clinical trial.

Then, Dr. Julia Busik, Professor and Chair of the Department of Biochemistry and Physiology at the University of Oklahoma College of Medicine, explains how an antibody was developed to prevent ceramide buildup in treating diabetic retinopathy in animal and cell models.

8/4/2024 Podcast (Click Image Below)